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Enhanced transgene expression from single-stranded AAV vectors in human cells in vitro and in murine hepatocytes in vivo
Author:
Yuan Lu, Chen Ling, Jakob Shoti, Hua Yang, Aneesha Nath, Geoffrey D. Keeler, Keyun Qing, Arun Srivastava
Journal: Molecular Therapy
Apr 23 2024 -
Bilateral gene therapy in children with autosomal recessive deafness 9: single-arm trial results
Author:
Hui Wang, Jun Lv, Qi Cao, Longlong Zhang, Min Shen, Mengzhao Xun, Honghai Tang, Chong Cui, Yanbo Yin, Yi Zhou, Ziwen Gao, Sha Yu, Jinghan Wang, Wuqing Wang, Huawei Li & Yilai Shu
Journal: Nature Medicine
Jan 5 2024 -
Bi-directional communication between intrinsic enteric neurons and ILC2s inhibits host defense against helminth infection
Author:
Yinsheng Wang, Shaorui Liu, Zijia Sun, Xiaobao Huang, Qiang Wang, Ruichao Liu, Hongkai Xu, Tao Wu, Yu Li, Zirun Tang, Li Wu, Xiaohuan Guo, Lei Zhou, Hai Qi, Coco Chu
Journal: Immunity
Feb 11 2025 -
Brain‐Wide Neuroregenerative Gene Therapy Improves Cognition in a Mouse Model of Alzheimer’s Disease
Author:
Zheng Wu, Yu Xie, Shreya Swaminathan, Wenyu Ji, Yaowei Guo, Gong Chen
Journal: Advanced Science
Feb 14 2025 -
CRISPR-Cas9-mediated genome editing delivered by a single AAV9 vector inhibits HSV-1 reactivation in a latent rabbit keratitis model
Author:
Nadia Amrani, Kevin Luk, Pankaj Singh, Mason Shipley, Meltem Isik, Martina Donadoni, Anna Bellizzi, Kamel Khalili, Ilker K. Sariyer, Donna Neumann, Jennifer Gordon, Guo-Xiang Ruan
Journal: Molecular Therapy
Doi: https://www.doi.org/10.1016/j.omtm.2024.101303
Aug 14 2024 -
Nucleus accumbens ghrelin signaling controls anxiety-like behavioral response to acute stress
Author:
Leilei Chang, Yecheng He, Tian Tian & Bin Li
Journal: Behavioral and Brain Functions
Doi: https://www.doi.org/10.1186/s12993-024-00244-z
Jul 4 2024 -
A nonhuman primate model with Alzheimer’s disease-like pathology induced by hippocampal overexpression of human tau
Author:
Zhouquan Jiang, Jing Wang, Yongpeng Qin, Shanggong Liu, Bin Luo, Fan Bai, Huiyi Wei, Shaojuan Zhang, Junjie Wei, Guoyu Ding, Long Ma, Shu He, Rongjie Chen, Ying Sun, Yi Chen, Lu Wang, Hao Xu, Xiangyu Wang, Gong Chen & Wenliang Lei
Journal: Alzheimers Research & Therapy
Doi: https://www.doi.org/10.1186/s13195-024-01392-0
Jan 27 2024 -
Adeno-Associated Virus-Mediated Dorsal Root Ganglion Toxicity in the New Zealand White Rabbit
Author:
Eric Tien, Branka Grubor, Melissa Kirkland, Su Jing Chan, Nick van der Munnik, Wenlong Xu, Kate Henry, Stefan Hamann, Cong Wei, Wan-Hung Lee, Davide Gianni, Ashton Brennecke, Kalyani Nambiar, Jeron Chen, Bin Liu, Shen Shen, Claudine Tremblay, Edward D. Plowey, Patrick Trapa, James Fikes, Junghae Suh, and Dale Morris
Journal: Toxicologic Pathology
Doi: https://www.doi.org/10.1177/01926233241229808
Feb 22 2024 -
Distributional comparison of different AAV vectors after unilateral cochlear administration
Author:
Shuang Han, Zhijiao Xu, Shengyi Wang, Honghai Tang, Shaowei Hu, Hui Wang, Guofang Guan & Yilai Shu
Journal: Gene Therapy
Doi: https://www.doi.org/10.1038/s41434-023-00431-z
Dec 14 2023 -
A micro-electroporation/electrophoresis-based vaccine screening system reveals the impact of vaccination orders on cross-protective immunity
Author:
Yongyong Li, Jingshan Mo, Jing Liu, Ying Liang, Caiguanxi Deng, Zhangping Huang, Juan Jiang, Ming Liu, Xinmin Liu, Liru Shang, Xiafeng Wang, Xi Xie, Ji Wang
Journal: iScience
Doi: https://www.doi.org/10.1016/j.isci.2023.108086
Sep 27 2023 -
Cas12n nucleases, early evolutionary intermediates of type V CRISPR, comprise a distinct family of miniature genome editors
Author:
Weizhong Chen, Jiacheng Ma, Zhaowei Wu, Zhipeng Wang, Hongyuan Zhang, Wenhan Fu, Deng Pan, Jin Shi, Quanjiang Ji
Journal: Molecular Cell
Doi: https://www.doi.org/10.1016/j.molcel.2023.06.014
Jul 03 2023 -
Efficient Modulation of Exon Skipping via Antisense Circular RNAs
Author:
Shuaiwei Ren, Mei Huang, Raoxian Bai, Lijiao Chen, Jiao Yang, Junyu Zhang, Wenting Guo, Weizhi Ji, and Yongchang Chen
Journal: Research (Wash D C)
Doi: https://www.doi.org/10.34133/research.0045
Jan 19 2023